New detailed findings highlight the potential of an investigational form of our spinal muscular atrophy (SMA) therapy. These data will be presented in a session at the Annual Congress of the World Muscle Society by Thomas Crawford, M.D., co-director, Muscular Dystrophy Association Clinic at Johns Hopkins Medicine. Learn more about our latest research: https://ow.ly/QqlX50THSXX | Biogen
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Gene Therapy for Spinal Muscular Atrophy (SMA)
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Gene therapy company begins operations in Longmont
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Today, the Food and Drug Administration approved a new gene therapy for Spinal Muscular Atrophy. SMA Type 1 is the number one genetic killer of children 2 and under. This first-time gene therapy, developed here at Nationwide Children's, is allowing kids like Evelyn to have a bright future. Watch her incredible story. | Nationwide Children's Hospital
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