KERA News

Texas is screening for more rare diseases in babies, but families still face barriers to treatment

Since the 1960s, Texas has screened newborns for a variety of rare diseases — like sickle cell anemia and cystic fibrosis.
Nasdaq

FDA Accepts REGENXBIO's BLA For RGX-121 In Hunter Syndrome; Grants Priority Review

(RTTNews) - REGENXBIO Inc. (RGNX) Tuesday said that the U.S. Food and Drug Administration (FDA) has accepted the Biologics License Application (BLA) for RGX-121 for the treatment of ...

Takeda Pharmaceutical unveils $170M expansion in Thousand Oaks

Takeda employs 500 people in Thousand Oaks. For the past four years, it has been working on a $170 million expansion and ...
MarketWatch

Regenxbio Shares Rise on Positive Long-Term Data for Hunter Syndrome Drug

Regenxbio shares rose in early trading Friday after it revealed positive long-term data for the trials of its Hunter syndrome treatment. Shares rose 4.7% higher to $9.86. The biotechnology company ...
Insider Monkey

Denali Therapeutics Inc. (DNLI) Secures FDA Priority Review for First-Ever Brain-Penetrant Hunter Syndrome Therapy

We recently compiled a list of 11 Best Future Stocks to Buy Now. Denali Therapeutics Inc. stands sixth on our list among the best future stocks. Denali Therapeutics Inc. (NASDAQ:DNLI) is a ...