Recordati Rare Diseases Inc. today announced the presentation of real-world data that build upon the safety data of sutimlimab, an FDA-approved therapy for hemolysis in adults with cold agglutinin ...
Rare diseases affect fewer than 200,000 people in the U.S., approximately 30 million individuals. Sadly, 3 out of 10 children with a rare disease won’t live to see their fifth birthday, yet the path ...
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AI detects rare diseases from voice
Artificial Intelligence (AI) is significantly impacting the healthcare sector, particularly in diagnosing rare diseases. One of the most intriguing advancements is AI’s newfound ability to detect ...
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‘Our kids don’t have time’: NC parents, researchers urge FDA to act quickly on drugs for rare diseases
RALEIGH, N.C. (WNCN) – Parents of children with ultra-rare diseases are encouraging the Food and Drug Administration to act quickly to approve drugs that could treat their conditions and to take into ...
The National Institutes of Health established the Genomics Research to Elucidate the Genetics of Rare Diseases (GREGoR) Consortium in 2021 with the goal of finding molecular diagnoses for individuals ...
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