"My medicine is making me stronger," 7-year-old Hudson Sanford says after receiving a breakthrough gene therapy for Duchenne Muscular Dystrophy Cara Lynn Shultz is a writer-reporter at PEOPLE. Her ...
CLEVELAND, Ohio — Stand-up comedian and actor Gilbert Gottfried, who died this week at 67, lived for years with the rare genetic muscle disorder myotonic dystrophy type 2, a common form of muscular ...
Sarepta says it has what could be the first gene therapy for limb girdle muscular dystrophy. But approval is going to be ...
The first gene therapy for children with Duchenne muscular dystrophy has been approved by the U.S. Food and Drug Administration. The therapy can be used in 4- and 5-year-olds with the degenerative ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback