Deaf children can now hear thanks to a new treatment that repairs a defective gene. Researchers associated with the biotech company Regeneron Pharmaceuticals unveiled the successful gene therapy last ...

Researchers have developed a modified version of the CRISPR gene-editing tool that in early laboratory experiments suggests ...

Following its FDA-approved Casgevy therapy for sickle cell disease and beta thalassemia, CRISPR technology is now being tested in autoimmune disorders and early Down syndrome studies. CRISPR ...

Gene editing techniques may eventually allow trisomy to be treated at the cellular level, according to an in vitro proof-of-concept study. Down syndrome is caused by the presence of a third copy of ...